Cell and gene therapy encompasses a broad range of therapeutic interventions for diseases that have proved refractory to treatment with…

The groundbreaking partnership that successfully treated a rare metabolic disorder in KJ Muldoon, or “Baby KJ,” with personalized CRISPR therapy…

Cartoon schematic of a lipid nanoparticle (LNP) illustrating typical component lipids and internal organization. In contrast to classical liposomes, LNPs…

According to the American Brain Foundation, over one in three people around the world are affected by neurological conditions, the…

Ajay Gannerkote, president of Integrated DNA Technologies (IDT), says what’s most exciting about CRISPR is its potential to shift medicine…

As cell and gene therapies (CGTs) move from the research stage to commercial applications, biomanufacturers are seeing that many of…

Gene therapy has entered a complicated phase. Over the past several years, the field has delivered remarkable scientific breakthroughs alongside…

Edmund ChampnessCSO, Company DirectorOptibrium In early-phase drug discovery, we do a good job of tracking the obvious productivity metrics, like…

Fouad Atouf, PhD Chief Science OfficerUnited States Pharmacopeia (USP) Documentary standards such as monographs, general chapters, and reference standards are…

Inflammation is at the core of many diseases. Yet, although many therapeutics have been developed to treat inflammatory diseases, they…